Advancing medicines for patients living with rare and serious diseases drives everything we do. Our science is rooted in finding potential solutions for difficult-to-treat conditions that traditionally have been overlooked and underserved.
By challenging the status quo, our research vision is to bring forth an innovative and robust pipeline of potential new therapies that bring hope to patients who need it most.
Our journey to innovation relies on the diverse expertise of our in-house scientists as well as exploration of external opportunities to achieve our mission.
"Our goal is to go where others aren't, to blaze new trails, and to bring together multiple technologies to create drugs that have the potential to advance patient care. That's what sets us apart."
Walter Perkins, Ph.D., Chief Technology Officer
We are committed to developing scientific innovations in house as well as exploring external opportunities to achieve our mission.