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Synthetic Rescue

Identifying new drug targets for genetic diseases

Despite ongoing advances in genetic technologies, the successful treatment of many genetic diseases remains out of reach.

Our leading synthetic rescue platform enables us to identify targets for potential drug development that are outside the disrupted biological pathway which, when modulated, have the potential to restore cell health. This scalable platform couples cutting-edge molecular and cell biology techniques with sophisticated analysis of human genetics datasets.

Find out how our leading synthetic rescue platform couples cutting-edge molecular and cell biology techniques with sophisticated analysis of human genetics datasets to identify targets for potential drug development in a range of diseases.

Gene Therapy with Targeted Delivery

Learn More

Protein Deimmunization

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RNA End-Joining Technology

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Proprietary Manufacturing

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